Lumacaftor is a medication used to treat individuals with cystic fibrosis, a genetic disorder that affects the lungs and digestive system. It works by helping to correct the misfolded protein caused by the CFTR gene mutation, improving the function of the protein and enhancing the movement of salt and water in and out of cells. Typically prescribed in combination with Ivacaftor, Lumacaftor is taken orally and is intended for patients who have specific mutations in the CFTR gene. This treatment can help reduce symptoms and improve lung function, ultimately enhancing the quality of life for those affected by cystic fibrosis.