cysteamine
Cysteamine is a medication primarily used to treat cystinosis, a rare genetic disorder that leads to the accumulation of the amino acid cystine in cells. By reducing cystine levels, cysteamine helps prevent damage to organs, particularly the kidneys and eyes. It is available in various forms, including capsules and eye drops.
In addition to its use in cystinosis, cysteamine has been studied for potential benefits in other conditions, such as neurodegenerative diseases and metabolic disorders. However, its primary application remains in managing cystinosis, where it plays a crucial role in improving patients' quality of life.