Spinraza
Spinraza is a medication used to treat spinal muscular atrophy (SMA), a genetic disorder that affects muscle strength and movement. It works by increasing the production of a protein called survival motor neuron (SMN), which is essential for the health of motor neurons in the spinal cord.
Administered through an injection into the spinal canal, Spinraza is typically given in a series of doses. It is approved for use in patients of all ages, including infants, and aims to improve motor function and quality of life for those affected by SMA.